Gene Therapy Advances in Treating Neurodegenerative Disorders
Introduction Neurodegenerative disorders are among the most complex diseases of modern medicine. They are characterized by progressive loss in the …
CRISPR/Cas9
Gene Therapy for Hemophilia: Progress, Challenges, and Future Directions
Introduction Hemophilia is an inherited disorder producing a deficiency of clotting factors, either factor VIII or factor IX, and has …