There have been several notable successes in gene therapy:
Severe Combined Immunodeficiency (SCID): Gene therapy has successfully treated children with SCID, also known as "bubble boy" disease, by introducing a functional copy of the defective gene. Leber's Congenital Amaurosis: Patients with this inherited form of blindness have regained vision following gene therapy treatments. Hemophilia: Recent advancements have led to successful gene therapy treatments for Hemophilia A and B, allowing patients to produce the clotting factors they lack.
